In vivo delivery of human acid ceramidase via cord blood transplantation and direct injection of lentivirus as novel treatment approaches for Farber disease-Reference-Cited by-同舟云学术

In vivo delivery of human acid ceramidase via cord blood transplantation and direct injection of lentivirus as novel treatment approaches for Farber disease

Published:2008-11 Issue:3 Volume:95 Page:133-141
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Ramsubir Shobha,Nonaka Takahiro,Girbés Carmen Bedia,Carpentier Stéphane,Levade Thierry,Medin Jeffrey A.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference49 articles.

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4. Acid ceramidase deficiency: farber lipogranulomatosis;Moser,2001

5. Molecular analysis of acid ceramidase deficiency in patients with Farber disease;Bar;Hum. Mutat.,2001

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