Long-term hematological, visceral, and growth outcomes in children with Gaucher disease type 3 treated with imiglucerase in the International Collaborative Gaucher Group Gaucher Registry-Reference-Cited by-同舟云学术

Long-term hematological, visceral, and growth outcomes in children with Gaucher disease type 3 treated with imiglucerase in the International Collaborative Gaucher Group Gaucher Registry

Published:2017-01 Issue:1-2 Volume:120 Page:47-56
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

El-Beshlawy Amal,Tylki-Szymanska Anna,Vellodi Ashok,Belmatoug Nadia^ORCID,Grabowski Gregory A.,Kolodny Edwin H.,Batista Julie L.,Cox Gerald F.,Mistry Pramod K.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

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