Two years of pegvaliase in Germany: Experiences and best practice recommendations-Reference-Cited by-同舟云学术

Two years of pegvaliase in Germany: Experiences and best practice recommendations

Published:2023-05 Issue:1 Volume:139 Page:107564
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Krämer Johannes,Baerwald Christoph,Heimbold Christian,Kamrath Clemens,Parhofer Klaus G.,Reichert Anja,Rutsch Frank,Stolz Simone,Weinhold Natalie,Muntau Ania C.

Funder

BioMarin Pharmaceutical Inc

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference43 articles.

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2. The complete European guidelines on phenylketonuria: diagnosis and treatment;van Wegberg;Orphanet. J. Rare Dis.,2017

3. Pegvaliase for the treatment of phenylketonuria: results of a long-term phase 3 clinical trial program (PRISM);Thomas;Mol. Genet. Metab.,2018

4. PKU dietary handbook to accompany PKU guidelines;MacDonald;Orphanet. J. Rare Dis.,2020

5. Adherence to clinic recommendations among patients with phenylketonuria in the United States;Jurecki;Mol. Genet. Metab.,2017

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