Favourable effect of early versus late start of enzyme replacement therapy on plasma globotriaosylsphingosine levels in men with classical Fabry disease-Reference-Cited by-同舟云学术

Favourable effect of early versus late start of enzyme replacement therapy on plasma globotriaosylsphingosine levels in men with classical Fabry disease

Published:2017-06 Issue:2 Volume:121 Page:157-161
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Arends Maarten,Wijburg Frits A.,Wanner Christoph,Vaz Frédéric M.,van Kuilenburg André B.P.,Hughes Derralynn A.,Biegstraaten Marieke,Mehta Atul,Hollak Carla E.M.,Langeveld Mirjam

Funder

ZonMw

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference26 articles.

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5. Long term enzyme replacement therapy for Fabry disease: effectiveness on kidney, heart and brain;Rombach;Orphanet J. Rare Dis.,2013

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