Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study-Reference-Cited by-同舟云学术

Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study

Published:2024-04 Issue: Volume:39 Page:100862
ISSN:2666-7762
Container-title:The Lancet Regional Health - Europe
language:en
Short-container-title:The Lancet Regional Health - Europe

Author:

Günther René,Wurster Claudia Diana,Brakemeier Svenja,Osmanovic Alma,Schreiber-Katz Olivia,Petri Susanne,Uzelac Zeljko,Hiebeler Miriam,Thiele Simone,Walter Maggie C.,Weiler Markus^ORCID,Kessler Tobias,Freigang Maren,Lapp Hanna Sophie,Cordts Isabell,Lingor Paul^ORCID,Deschauer Marcus,Hahn Andreas,Martakis Kyriakos^ORCID,Steinbach Robert,Ilse Benjamin,Rödiger Annekathrin,Bellut Julia,Nentwich Julia,Zeller Daniel,Muhandes Mohamad Tareq,Baum Tobias,Christoph Koch Jan,Schrank Bertold,Fischer Sophie,Hermann Andreas^ORCID,Kamm Christoph,Naegel Steffen,Mensch Alexander,Weber Markus,Neuwirth Christoph,Lehmann Helmar C.,Wunderlich Gilbert,Stadler Christian,Tomforde Maike,George Annette,Groß Martin,Pechmann Astrid,Kirschner Janbernd,Türk Matthias,Schimmel Mareike,Bernert Günther,Martin Pascal,Rauscher Christian,Meyer zu Hörste Gerd,Baum Petra,Löscher Wolfgang,Flotats-Bastardas Marina,Köhler Cornelia,Probst-Schendzielorz Kristina,Goldbach Susanne,Schara-Schmidt Ulrike,Müller-Felber Wolfgang,Lochmüller Hanns,von Velsen Otgonzul,Kleinschnitz Christoph,Ludolph Albert C.,Hagenacker Tim^ORCID

Funder

Universitätsklinikum Essen

Roche

Novartis Pharma AG

Biogen Inc

Novartis

Publisher

Elsevier BV

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3. Muscle strength and motor function throughout life in a cross-sectional cohort of 180 patients with spinal muscular atrophy types 1c-4;Wadman;Eur J Neurol,2018

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1. Nusinersen Improves Motor Function in Type 2 and 3 Spinal Muscular Atrophy Patients across Time;Biomedicines;2024-08-06

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3. Beyond Motor Neurons in Spinal Muscular Atrophy: A Focus on Neuromuscular Junction;International Journal of Molecular Sciences;2024-07-03