LinQURE: A novel AAV gene silencing platform that supports multi-transcript targeting for complex disorders
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Published:2024-09
Issue:3
Volume:35
Page:102307
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ISSN:2162-2531
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Container-title:Molecular Therapy - Nucleic Acids
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language:en
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Short-container-title:Molecular Therapy - Nucleic Acids
Author:
Bočkaj Irena,
Moreno Garcia Anna,
de Miguel Herraiz Pablo,
Keskin Sonay,
Zancanella Vanessa,
Acar Broekmans Şeyda,
Vallès Astrid,
Liu Ying Poi,
Evers Melvin,
Wartel MorganeORCID