Targeting DMPK with Antisense Oligonucleotide Improves Muscle Strength in Myotonic Dystrophy Type 1 Mice-Reference-Cited by-同舟云学术

Targeting DMPK with Antisense Oligonucleotide Improves Muscle Strength in Myotonic Dystrophy Type 1 Mice

Published:2017-06 Issue: Volume:7 Page:465-474
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Jauvin Dominic,Chrétien Jessina,Pandey Sanjay K.,Martineau Laurie,Revillod Lucille,Bassez Guillaume,Lachon Aline,MacLeod A. Robert,Gourdon Geneviève,Wheeler Thurman M.,Thornton Charles A.,Bennett C. Frank,Puymirat Jack

Funder

Ionis Pharmaceuticals, Inc.

Muscular Dystrophy Association

Canada Foundation for Innovation (CFI)

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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4. Maturational arrest of fetal muscle in neonatal myotonic dystrophy. A pathologic study of four cases;Sarnat;Arch. Neurol.,1976

5. Myotonic dystrophy;Thornton;Neurol. Clin.,2014

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