EXPERTS COUNCIL RESOLUTION. RESULTS OF MPS I PATIENTS MONITORING. CRITERIA FOR ERT TREATMENT RE-INITIATION IN MPS I AFTER HSCT-Reference-Cited by-同舟云学术

EXPERTS COUNCIL RESOLUTION. RESULTS OF MPS I PATIENTS MONITORING. CRITERIA FOR ERT TREATMENT RE-INITIATION IN MPS I AFTER HSCT

Published:2022-07-05 Issue:3 Volume:19 Page:291-293
ISSN:2500-3089
Container-title:Pediatric pharmacology
language:
Short-container-title:Pediatr. farmakol.

Author:

Editorial Article

Abstract

Publisher

Paediatrician Publishers LLC

Subject

Pulmonary and Respiratory Medicine,Pediatrics, Perinatology and Child Health

Reference15 articles.

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2. Boffi L, Russo P, Limongelli G. Early diagnosis and management of cardiac manifestations in mucopolysaccharidoses: a practical guide for paediatric and adult cardiologists. Ital J Pediatr. 2018;44 (Suppl 2):122. doi: https://doi.org/10.1186/s13052-018-0560-3

3. Vasichkina ES, Vershinina TL, Kovalchuk TS, et al. Damages of Cardiovascular System at Mucopolysaccharidosis Type I: Clinical Cases. Voprosy sovremennoi pediatrii — Current Pediatrics. 2019;18(5):346–353. (In Russ). doi: https://doi.org/10.15690/vsp.v18i5.2058

4. Mikhaylova SV, Slateckay AN, Pristanskova EA, et al. Mucopolysaccharidosis I type: new management. Pediatric Hematology/Oncology and Immunopathology. 2018;17(4):35–42. (In Russ). doi: https://doi.org/10.24287/1726-1708-2018-17-4-35-42

5. Bykova TA, Ovechkina VN, Osipova AA, et al. An evaluation of the efficacy of allogeneic hematopoietic stem cell transplantation in patients with mucopolysaccharidosis type I (Hurler syndrome): the experience of the R.M. Gorbacheva Research Institute for Pediatric Oncology, Hematology and Transplantation. Pediatric Hematology/ Oncology and Immunopathology. 2020;19(2):83–92. (In Russ). doi: https://doi.org/10.24287/1726-1708-2020-19-2-83-92

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