Newborn Screening and Emerging Therapies for X-Linked Adrenoleukodystrophy
Author:
Affiliation:
1. Kennedy Krieger Institute, Baltimore, Maryland
Publisher
American Medical Association (AMA)
Subject
Neurology (clinical)
Reference10 articles.
1. Adrenoleukodystrophy: neuroendocrine pathogenesis and redefinition of natural history.;Kemp;Nat Rev Endocrinol,2016
2. Adrenoleukodystrophy: incidence, new mutation rate, and results of extended family screening.;Bezman;Ann Neurol,2001
3. Newborn screening for X-linked adrenoleukodystrophy.;Moser;Int J Neonatal Screen,2016
4. X-Linked adrenoleukodystrophy: overview and prognosis as a function of age and brain magnetic resonance imaging abnormality: a study involving 372 patients.;Moser;Neuropediatrics,2000
5. Analysis of MRI patterns aids prediction of progression in X-linked adrenoleukodystrophy.;Loes;Neurology,2003
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