Gene Replacement Therapy Rescues Photoreceptor Degeneration in a Murine Model of Leber Congenital Amaurosis Lacking RPGRIP-Reference-Cited by-同舟云学术

Gene Replacement Therapy Rescues Photoreceptor Degeneration in a Murine Model of Leber Congenital Amaurosis Lacking RPGRIP

Published:2005-09-01 Issue:9 Volume:46 Page:3039
ISSN:1552-5783
Container-title:Investigative Opthalmology & Visual Science
language:en
Short-container-title:Invest. Ophthalmol. Vis. Sci.

Author:

Pawlyk Basil S.¹,Smith Alexander J.²,Buch Prateek K.²,Adamian Michael¹,Hong Dong-Hyun¹,Sandberg Michael A.¹,Ali Robin R.²,Li Tiansen¹

Affiliation:

1. From the Berman-Gund Laboratory for the Study of Retinal Degenerations, Harvard Medical School, Massachusetts Eye and Ear Infirmary, Boston, Massachusetts; the

2. Division of Molecular Therapy, Institute of Ophthalmology, University College London, London, United Kingdom.

Publisher

Association for Research in Vision and Ophthalmology (ARVO)

Subject

General Medicine

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