Author:
Harmatz P,Kramer W,Hopwood J,Simon J,Butensky E,Swiedler S
Subject
General Medicine,Pediatrics, Perinatology, and Child Health
Reference14 articles.
1. Neufeld, E and Muenzer, J.(2001) The mucopolysaccharidoses. In The metabolic and molecular basis of inherited disease8th. ( pp. 3412 - 52 ). New York : McGraw-Hill.
2. Krivit, W. (1992) Maroteaux-Lamy Syndrome (Mucopolysaccharidosis Type VI). Treatment by allogeneic bone marrow transplantation in 6 subjects and potential for autotransplantation bone marrow gene insertion Int Pediatr, 7, pp. 42 - 52.
3. Krivit, W and Pierpont, M and Ayaz, K and Tsai, M and Ramsay, N and Kersey, J and (1984) Bone-marrow transplantation in the Maroteaux-Lamy syndrome (mucopolysaccharidosis type VI). Biochemical and clinical status 24 months after transplantation N Engl J Med, 311, pp. 1606 - 11.
4. Hoogerbrugge, P and Brouwer, O and Bordigoni, P and Ringden, O and Kapaun, P and Ortega, J and (1995) Allogeneic bone marrow transplantation for lysosomal storage diseases. The European Group for Bone Marrow Transplantation Lancet, 345, pp. 1398 - 402.
5. Wraith, J. (2001) Advances in the treatment of lysosomal storage disease Dev Med Child Neurol, 43, pp. 639 - 46.
Cited by
47 articles.
订阅此论文施引文献
订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献