Liver-directed gene-based therapies for inborn errors of metabolism
Author:
Affiliation:
1. Telethon Institute of Genetics and Medicine, Pozzuoli, Italy
2. Department of Translational Medicine, Federico II University of Naples, Naples, Italy
Funder
Telethon Foundation
Publisher
Informa UK Limited
Subject
Clinical Biochemistry,Drug Discovery,Pharmacology
Link
https://www.tandfonline.com/doi/pdf/10.1080/14712598.2020.1817375
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