Tissue distribution of renadirsen sodium, a dystrophin exon-skipping antisense oligonucleotide, in heart and diaphragm after subcutaneous administration to cynomolgus monkeys-Reference-Cited by-同舟云学术

Tissue distribution of renadirsen sodium, a dystrophin exon-skipping antisense oligonucleotide, in heart and diaphragm after subcutaneous administration to cynomolgus monkeys

Published:2024-08-10 Issue: Volume: Page:1-17
ISSN:1525-7770
Container-title:Nucleosides, Nucleotides & Nucleic Acids
language:en
Short-container-title:Nucleosides, Nucleotides & Nucleic Acids

Author:

Yamamura Naotoshi¹,Takakusa Hideo¹,Asano Daigo¹,Watanabe Kyoko¹,Shibaya Yukari¹,Yamanaka Ryo²,Fusegawa Keiichi²,Kanda Akira³,Nagase Hiroyuki³,Takaishi Kiyosumi³,Koizumi Makoto⁴,Takeshima Yasuhiro⁵,Matsuo Masafumi⁶

Affiliation:

1. Drug Metabolism & Pharmacokinetics Research Laboratories, Daiichi Sankyo Co., Ltd, Tokyo, Japan

2. Research & Innovation Promotion Department, Daiichi Sankyo Co., Ltd, Tokyo, Japan

3. Specialty Medicine Research Laboratories I, Daiichi Sankyo Co., Ltd, Tokyo, Japan

4. Modality Research Laboratories, Daiichi Sankyo Co., Ltd, Tokyo, Japan

5. Department of Pediatrics, Hyogo College of Medicine, Nishinomiya, Japan

6. Faculty of Health Sciences, Kobe Tokiwa University, Kobe, Japan

Publisher

Informa UK Limited

Link

https://www.tandfonline.com/doi/pdf/10.1080/15257770.2024.2389545

Reference25 articles.

1. Newborn bloodspot screening for Duchenne Muscular Dystrophy: 21 years experience in Wales (UK)

2. Duchenne muscular dystrophy and dystrophin: pathogenesis and opportunities for treatment

3. The structural and functional diversity of dystrophin

4. Comprehensive Detection of Genomic Duplications and Deletions in the DMD Gene, by Use of Multiplex Amplifiable Probe Hybridization

5. Cardiac and respiratory involvement in advanced stage Duchenne muscular dystrophy