1. Australian Government Department of Health. Pharmaceutical Benefits Scheme—hepatitis C medicines 2016. Canberra (ACT); 2016.
2. Australian Minister for Health. PBS listing for Kalydeco and Soliris. Canberra (ACT): The Hon Peter Dutton MP Minister for Health; 2014.
3. Australian Government Department of Health. Application 1519: tisagenlecleucel (CTL019) for treatment of refractory/relapsed CD19-positive leukaemia and lymphoma. PICO confirmation: Medical Services Advisory Committee; 2018 (last updated: 25 Jun 2018).
http://www.msac.gov.au/internet/msac/publishing.nsf/Content/1519-public
. Accessed 10 Jan 2019.
4. Liu G, Chen E, Lewis D, Rao G. Food and Drug Administration’s Humanitarian Device Exemption marketing approval pathway: insights for developing devices for rare diseases. J Med Devices. 2017;11:034701–034708.
https://doi.org/10.1115/1.4036333
.
5. Australian Government Department of Health. Prostheses list: part A. Canberra (ACT): Australian Government Department of Health; 2018.