Onasemnogene Abeparvovec for Treating Pre-symptomatic Spinal Muscular Atrophy: An External Assessment Group Perspective of the Partial Review of NICE Highly Specialised Technology Evaluation 15-Reference-Cited by-同舟云学术

Onasemnogene Abeparvovec for Treating Pre-symptomatic Spinal Muscular Atrophy: An External Assessment Group Perspective of the Partial Review of NICE Highly Specialised Technology Evaluation 15

Published:2023-09-20 Issue:6 Volume:7 Page:863-875
ISSN:2509-4262
Container-title:PharmacoEconomics - Open
language:en
Short-container-title:PharmacoEconomics Open

Author:

Chaplin Marty^ORCID,Bresnahan Rebecca^ORCID,Fleeman Nigel^ORCID,Mahon James^ORCID,Houten Rachel^ORCID,Beale Sophie^ORCID,Boland Angela^ORCID,Dundar Yenal^ORCID,Marsden Ashley,Munot Pinki^ORCID

Funder

Evidence Synthesis Programme

Publisher

Springer Science and Business Media LLC

Subject

Pharmacology (medical),Health Policy,Pharmacology

Link

https://link.springer.com/content/pdf/10.1007/s41669-023-00439-6.pdf

Reference44 articles.

1. National Institute for Health and Care Excellence. Highly specialised technologies guidance. 2023; Available at: https://www.nice.org.uk/About/What-we-do/Our-Programmes/NICE-guidance/NICE-highly-specialised-technologies-guidance. Accessed 12 July 2023.

2. National Institute for Health and Care Excellence. Onasemnogene abeparvovec for treating spinal muscular atrophy: Highly specialised technologies guidance [HST15]. 2021; Available at: https://www.nice.org.uk/guidance/hst15. Accessed 12 July 2023.

3. National Institute for Health and Care Excellence. Onasemnogene abeparvovec for treating presymptomatic spinal muscular atrophy: highly specialised technologies guidance [HST24]. 2023. Available at: https://www.nice.org.uk/guidance/hst24. Accessed 12 July 2023.

4. Kolb SJ, Kissel JT. Spinal muscular atrophy. Neurol Clin. 2015;33(4):831–46.

5. Kolb SJ, Coffey CS, Yankey JW, Krosschell K, Arnold WD, Rutkove SB, et al. Natural history of infantile-onset spinal muscular atrophy. Ann Neurol. 2017;82(6):883–91.

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