Eladocagene Exuparvovec: First Approval-Reference-Cited by-同舟云学术

Eladocagene Exuparvovec: First Approval

Published:2022-09-14 Issue: Volume: Page:
ISSN:0012-6667
Container-title:Drugs
language:en
Short-container-title:Drugs

Author:

Keam Susan J.

Publisher

Springer Science and Business Media LLC

Subject

Pharmacology (medical)

Link

https://link.springer.com/content/pdf/10.1007/s40265-022-01775-3.pdf

Reference17 articles.

1. Wassenberg T, Molero-Luis M, Jeltsch K, et al. Consensus guideline for the diagnosis and treatment of aromatic L-amino acid decarboxylase (AADC) deficiency. Orphanet J Rare Dis. 2017. https://doi.org/10.1186/s13023-016-0522-z.

2. Himmelreich N, Montioli R, Bertoldi M, et al. Aromatic amino acid decarboxylase deficiency: molecular and metabolic basis and therapeutic outlook. Mol Genet Metab. 2019;127(1):12–22.

3. Hwu PW, Kiening K, Anselm I, et al. Gene therapy in the putamen for curing AADC deficiency and Parkinson’s disease. EMBO Mol Med. 2021;13(9): e14712.

4. National Organisation for Rare Disorders Inc. Aromatic L-amino acid decarboxylase deficiency. 2021. https://rarediseases.org/. Accessed 8 Aug 2022.

5. European Medicines Agency. Eladocagene exuparvovec: EU summary of product characteristics 2022. https://ec.europa.eu/health/documents/community-register/html/h1653.htm. Accessed 25 July 2022

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