Long-term correction of hemorrhagic diathesis in hemophilia A mice by an AAV-delivered hybrid FVIII composed of the human heavy chain and the rat light chain-Reference-Cited by-同舟云学术

Long-term correction of hemorrhagic diathesis in hemophilia A mice by an AAV-delivered hybrid FVIII composed of the human heavy chain and the rat light chain

Published:2022-01-17 Issue:4 Volume:16 Page:584-595
ISSN:2095-0217
Container-title:Frontiers of Medicine
language:en
Short-container-title:Front. Med.

Author:

Mao Jianhua,Wang Yun,Zhang Wei,Shen Yan,Zhang Guowei,Xi Wenda,Wang Qiang,Ruan Zheng,Wang Jin,Xi Xiaodong

Publisher

Springer Science and Business Media LLC

Subject

General Medicine

Link

https://link.springer.com/content/pdf/10.1007/s11684-021-0844-7.pdf

Reference45 articles.

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2. Bolton-Maggs PHB, Pasi KJ. Haemophilias A and B. Lancet 2003; 361(9371): 1801–1809

3. Lai J, Hough C, Tarrant J, Lillicrap D. Biological considerations of plasma-derived and recombinant factor VIII immunogenicity. Blood 2017; 129(24): 3147–3154

4. Morfini M, Rapisarda CAP. Safety of recombinant coagulation factors in treating hemophilia. Expert Opin Drug Saf 2019; 18(2): 75–85

5. Perrin GQ, Herzog RW, Markusic DM. Update on clinical gene therapy for hemophilia. Blood 2019; 133(5): 407–414

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